Search Results
A Story of Hope and Fight for Life, Nella's Fight, Juvenile GM1 Gangliosidosis, GM1 EL-PFDD
The GM1 Gangliosidosis Externally-Led Patient-Focused Drug Development Meeting (EL-PFDD)
Hampus, Julia, and Isabella's GM1 Story - GM1 EL-PFDD
Honoring the Memory of Baby Dean and the Caruana Family
Jenny Bragg and Clara's GM1 Advocacy Story
Discussing the Cure GM1 Foundation, GM1 research & How to support families with rare disease
Hampus, Julia, and Isabella, Rare disease Day 2019
Positive Interim Data in Gene Therapy Trial for GM1 Gangliosidosis
Lysogene GM1 Gangliosidosis AAV Gene Therapy 2020
Save Our Sweet Girl Iris
LYS-GM101 AAV gene therapy for GM1 gangliosidosis
